Presentation
Anne graduated from University Pierre and Marie Curie (France) obtaining a Master degree in Biotechnology. She discovered her passion in gene therapy during an internship at uniQure (Netherlands) in 2017. Here, she worked on the implementation of a quantitative assay for AAV detection and the improvement of the packaging quality of transgenes in AAVs. In 2018, she joined the laboratory of Dr. Annarita Miccio as an junior research assistant working on the development of lentiviral and genome editing strategies for β-hemoglobinopathies. She is also working on the follow-up of gene-therapy treated patients in the Laboratory of Cellular and Gene Therapy led by Prof. Marina Cavazzana.
Resources & publications
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2022Journal (source)Nat MedLong-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: t...
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2022Journal (source)Nat CommunBase-editing-mediated dissection of a γ-globin cis-regulatory element for the...
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2023Journal (source)Mol Ther Nucleic AcidsNovel lentiviral vectors for gene therapy of sickle cell disease combining ge...
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2022Journal (source)Mol TherCombination of lentiviral and genome editing technologies for the treatment o...
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2021Journal (source)Blood AdvCorrection of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in h...